TRIALS: A Fight for Children with Niemann-Pick Type C, a Fatal Genetic Disease

National Niemann-Pick Disease Foundation, Inc. - October is Global Niemann- Pick Disease Awareness Month! For more information on Niemann-Pick Disease or to make a donation to NNPDF go to www.nnpdf.org

Elevation of plasma lysosphingomyelin-509 and urinary bile acid metabolite in Niemann-Pick disease type C-affected individuals - Top Articles selected by the Editor - Molecular Genetics and Metabolism Reports - Journal - Elsevier

Immune dysfunction in Niemann‐Pick disease type C - Platt - 2016 - Journal of Neurochemistry - Wiley Online Library

Niemann–Pick disease, type C - Wikipedia

Science Update: Biomarker for Niemann-Pick type C may be useful for diagnosing other class of rare disorders, NIH study suggests

Niemann-Pick Disease Type C Archives - The Children's Inn at NIH

NNPDF on X: #NNPDF partnered with @RareDiseases to create this animated educational resource on Niemann Pick Type C. Please help us raise awareness of #NPC by sharing this video with your networks

Niemann-Pick UK - GLOBAL NIEMANN-PICK DISEASE AWARENESS

SciELO - Brasil - Niemann-Pick disease type C: a case series of Brazilian patients Niemann-Pick disease type C: a case series of Brazilian patients

Ohio 2-year-old battling rare Niemann-Pick disease, dubbed 'childhood Alzheimer's