Generation of HEXA-deficient hiPSCs from fibroblasts of a Tay

Human iPSC line TSD-01-hiPSC was generated from fibroblasts of a patient with infantile Tay-Sachs disease (TSD). The patient is compound heterozygous …

Generation of HEXA-deficient hiPSCs from fibroblasts of a Tay-Sachs disease patient - ScienceDirect

Illustration of Tay-Sachs disease, a genetic disorder that progressively destroys brain neurons. It is caused by a mutation in the HEXA gene of chromo Stock Photo - Alamy

Frontiers The Linkage Phase of the Polymorphism KCNH2-K897T Influences the Electrophysiological Phenotype in hiPSC Models of LQT2

Presynaptic Dysfunction in Neurons Derived from Tay–Sachs iPSCs - ScienceDirect

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Adult mouse fibroblasts retain organ-specific transcriptomic identity

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Intranasal Delivery of CRISPR-Cas9 Edited HEXA Gene to Treat Tay Sachs Disease in Newborn HEXA/NEU3-Deficient Mice — Le Pouls

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PDF) Generation of HEXA-deficient hiPSCs from fibroblasts of a Tay-Sachs disease patient

Frontiers New Approaches to Tay-Sachs Disease Therapy