Diagnostic workup and management of patients with suspected Niemann-Pick type C disease - Apostolos Papandreou, Paul Gissen, 2016

PDF) Characterization of hydroxypropyl-beta-cyclodextrins used in the treatment of Niemann-Pick Disease type C1

Peter CLAYTON, University College London, London, UCL, Institute of Child Health

PDF) Characterization of hydroxypropyl-beta-cyclodextrins used in the treatment of Niemann-Pick Disease type C1

IJMS June-2 2023 - Browse Articles

IJMS June-2 2023 - Browse Articles

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PDF) Diagnostic workup and management of patients with suspected Niemann-Pick type C disease